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15-Sep-2021

Global Rare Disease Drugs Market is accounted for 0.8% CAGR by 2027 | Novartis AG,Hoffmann-La Roche Ltd.,Celgene Corporation,Bristol-Myers Squibb Company,Shire plc,Pfizer, Inc.,Sanofi S.A.,Bayer

Global Rare Disease Drugs Market report provides key enumeration on the Market status of the Global Rare Disease Drugs manufacturers and is a valuable source of guidance and direction for companies and individuals interested in the industry. The research was conducted using an objective combination of primary and secondary information including inputs from key participants in the Global Rare Disease Drugs industry. It delivers important information to identify and analyse the market need, market Growth and competition.

The global Global Rare Disease Drugs Market analysis further provides pioneering landscape of market along with market augmentation history and key development involved in the industry. The report also features comprehensive research study for high growth potential industries professional survey with market analysis. Global Rare Disease Drugs Market report helps the companies to understand the market trends and future market prospective,opportunities and articulate the critical business strategies.

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Rare diseases or orphan diseases at any time affect a small percentage of the population. The medicines indicated for the treatment of rare diseases are designated for orphan drugs. The drugs indicated for the treatment of rare diseases are designated for orphan drugs. According to the U.S. Food & Drug Administration (FDA), a disease or condition affecting around 200,000 people is defined as orphan disease in the U.S. Under the U.S. legislation, Orphan Drugs Act allows producers to ask U.S. FDA to grant medicines intended for the use of rare diseases or conditions to an orphan drug status. In the year 2017, according to U.S. FDA that the number of requests for orphan medicines designation has increased steadily in the last few years.

Due to various uncertainties associated with these diseases, the global rare diseases drugs market has been not considered lucrative until recently. Limited study possibilities provided a small percentage of the population affected. Due to the large differentiation and heterogeneity in a group of diseases that discouraged manufacturers from addressing unmet needs in this area, diseases were misunderstood. However, some high priced, highly unmet orphan drugs, such as the Spinraza, have attracted attention from manufacturers to the rare disease medication market at a price of US $125,000 per vial and high unmet requirements.

For 2016, total revenues of US$ 62.5 billion on the world’s top ten Global rare disease drugs market.

Novartis AG is a global pharmaceutical company with a diversified product portfolio that includes everything including cancer drug therapies to ophthalmic products. The company’s operations are managed by the Innovative Medicines Division, which includes the oncology and Novartis pharmaceutical business units. Innovative medicines Oncology division offers products for rare diseases and oncology diseases, and the pharmaceutical company includes neuroscience, ophthalmology, immunology and dermatology, cardio-metabolic, respiratory, and established medicines. In 2015, Novartis’ orphan drug Gleevec for the treatment of chronic myeloid leukaemia (CML) ended up losing its patent protection, and Sun Pharma released a generic Gleevec in 2016, putting a damper on Novartis’ Gleevec revenues.

Celgene Corporation is a pharmaceutical company that specializes in cancer and inflammatory disease treatments, such as Revlimid, Pomalyst, and Otezla. The company is currently focused on expanding the indication variety of its current therapies and has a strong pipeline of oncology treatments. For instance, Revlimid (lenalidomide) In phase III clinical trials for diffuse large B-cell lymphoma and follicular lymphoma, and indolent lymphoma. The company has additionally developed its own technological platforms for drug identification and discovery, allowing the company to quickly depart from target selection and validation to lead to identification and optimization.

Shire Plc. surpassed Pfizer Inc. as the global leader in orphan drug products (excluding oncology products) in 2016, grossing nearly US$ 11 billion. In 2016, Baxalta was acquired, along with its three therapeutic segments of hematology, immunology, and oncology. Shire Plc., which has invested US$ 1.4 billion in research and development, is also focused on providing therapies for rare diseases. The company had 37 therapies in development, and the Dyax and Baxalta acquisitions in 2016 enhanced the pipeline even more.

The global rare disease drugs market is influenced by a number of key trends that are driven by both supply and demand. The growing interest of manufacturers in providing therapies in this segment of the healthcare industry is due to a large gap between market needs and potential market offerings. Biopharma companies submitted 582 requests for orphan drug designation to the U.S. Food and Drug Administration (FDA) in 2016. Moreover, due to the availability of highly effective drug therapies, sales of orphan drug diseases have increased. Moreover, possible drug therapies for different types of cancer and rare diseases are in the pipeline, such as Tesaro, Inc.’s Niraparib, which is in phase I for the treatment of ovarian cancer, Roche’s Emicizumab, which is in phase III for the treatment of hemophilia, and Bluebird Bio’s LentiGlobin, which is in various stages for the treatment of sickle cell anemia and beta-thalassemia major. Positive outcomes from these clinical trials are expected to alter the global rare disease drug market’s outlook in the near future.

This research provides a comprehensive competitive landscape and competitive analysis for the market’s leading players. This will help you understand how successful companies in this market operate and what their long-term goals are.

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Reasons to Purchase this Report

• Current and future of global Global Rare Disease Drugs Market outlook in the developed and emerging markets
• The segment that is expected to dominate the market as well as the segment which holds highest CAGR in the forecast period.
• Regions/countries that are expected to witness the fastest growth rates during the forecast period
• The latest developments, market shares, and strategies that are employed by the major market players

Global Rare Disease Drugs  Market – Competitive Landscape

Key players functioning in the global prosthetic liners market consists of Novartis AG,Hoffmann-La Roche Ltd.,Celgene Corporation,Bristol-Myers Squibb Company,Shire plc,Pfizer, Inc.,Sanofi S.A.,Bayer,Alexion Pharmaceuticals, Inc.,Biogen, Inc.

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Last Updated: 15-Sep-2021